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An Open-Label Extension (OLE) study of Tezacaftor/Ivacaftor (TEZ/IVA) in patients (PTS) ≥ 12 years with cystic fibrosis (CF) Homozygous for F508DEL-CFTR (F/F) or Heterozygous for F508DEL-CFTR and a residual function mutation (F/RF)

P Flume, R Fischer Biner, DG Downey, C Brown, M Jain, R Fischer, C de Boeck, D Campbell, X Wang, N Ahluwalia, CA Owen, C Wainwright · Pneumologie · Ausgabe S 01 S 01/2020

DOI 10.1055/s-0039-3403253

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Autor:innenP Flume, R Fischer Biner, DG Downey, C Brown, M Jain, R Fischer, C de Boeck, D Campbell, X Wang, N Ahluwalia, CA Owen, C Wainwright
ZeitschriftPneumologie
AusgabeS 01 S 01/2020
Jahrgang / SeitenJg. 74

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An Open-Label Extension (OLE) study of Tezacaftor/Ivacaftor (TEZ/IVA) in patients (PTS) ≥ 12 years with cystic fibrosis (CF) Homozygous for F508DEL-CFTR (F/F) or Heterozygous for F508DEL-CFTR and a residual function mutation (F/RF)

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P Flume, R Fischer Biner, DG Downey, C Brown, M Jain, R Fischer, C de Boeck, D Campbell, X Wang, N Ahluwalia, CA Owen, C Wainwright (2020) An Open-Label Extension (OLE) study of Tezacaftor/Ivacaftor (TEZ/IVA) in patients (PTS) ≥ 12 years with cystic fibrosis (CF) Homozygous for F508DEL-CFTR (F/F) or Heterozygous for F508DEL-CFTR and a residual function mutation (F/RF). Pneumologie, 74 (S 01 S 01). https://doi.org/10.1055/s-0039-3403253

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