CareLit · DOI-Nachweis · Zeitschrift für Orthopädie und Unfallchirurgie
Therapeutic genome editing with engineered nucleases
DOI 10.5482/hamo-16-09-0035
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Nachweis in CareLit
Autor:innenHaas, S.; Dettmer, V.; Cathomen, T.
ZeitschriftZeitschrift für Orthopädie und Unfallchirurgie
Ausgabe01/2017
Jahrgang / SeitenJg. 37 · S. 45 bis 52
Kernaussage aus der Literatur
Abstract-Vorschau
SummaryTargeted genome editing with designer nucleases, such as zinc finger nucleases, TALE nucleases, and CRISPR-Cas nucleases, has heralded a new era in gene therapy. Genetic disorders, which have not been amenable to conventional gene-addition-type gene therapy approaches, such as disorders with dominant inheritance or diseases caused by mutations in tightly regulated genes, can now be treated by precise genome s…
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Zitierempfehlung
Haas, S.; Dettmer, V.; Cathomen, T (2017) Therapeutic genome editing with engineered nucleases. Zeitschrift für Orthopädie und Unfallchirurgie, 37 (01), 45 bis 52. https://doi.org/10.5482/hamo-16-09-0035
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