CareLit Fachartikel

Clinical Outcome Study for Dysferlinopathy: Three years of natural history data for clinical trial readiness

V Straub, MK James, AG Mayhew, S Spuler, JW Day, KJ Jones, DX Bharucha-Goebel, E Salort Campana, A Pestronk, S Krause, MC Walter, C Paradas, T Stojkovic, M Yoshimura, E Bravver, J Díaz-Manera, E Pegoraro, J Mendell, K Bushby · Nervenheilkunde · 2019 · Heft 05

Dokument
1200376
CareLit-ID
Jahr
2019
Publikation
PDF
nein
Metadaten
DOI
ja
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Bibliografische Angaben

Zeitschrift
Nervenheilkunde
Autor:innen
V Straub, MK James, AG Mayhew, S Spuler, JW Day, KJ Jones, DX Bharucha-Goebel, E Salort Campana, A Pestronk, S Krause, MC Walter, C Paradas, T Stojkovic, M Yoshimura, E Bravver, J Díaz-Manera, E Pegoraro, J Mendell, K Bushby
Ausgabe
Heft 05 / 2019
Jahrgang 38
Seiten
–
Erschienen: 2019-05-01 00:00:00
ISSN
0722-1541

Zusammenfassung

Clinical Outcome Study for Dysferlinopathy: Three years of natural history data for clinical trial readiness

Schlagworte

Clinical Outcome Study Dysferlinopathy Three Years Natural History Trial Readiness Nervenheilkunde