CareLit Fachartikel
Clinical Outcome Study for Dysferlinopathy: Three years of natural history data for clinical trial readiness
V Straub, MK James, AG Mayhew, S Spuler, JW Day, KJ Jones, DX Bharucha-Goebel, E Salort Campana, A Pestronk, S Krause, MC Walter, C Paradas, T Stojkovic, M Yoshimura, E Bravver, J Díaz-Manera, E Pegoraro, J Mendell, K Bushby · Nervenheilkunde · 2019 · Heft 05
Dokument
1200376
CareLit-ID
Jahr
2019
Publikation
PDF
nein
Metadaten
DOI
ja
zitierfähig
Bibliografische Angaben
Zusammenfassung
Clinical Outcome Study for Dysferlinopathy: Three years of natural history data for clinical trial readiness
Schlagworte
Clinical
Outcome
Study
Dysferlinopathy
Three
Years
Natural
History
Trial
Readiness
Nervenheilkunde